News Livable Lives - Available October 25! October 23, 2024 HDYO Research Video - Wave Update October 11, 2024 NEW Research Video Series - uniQure Update October 05, 2024 LoQus23 Update October 02, 2024 FDA Grants Fast Track Designation to PTC518 Huntington's Disease Program September 26, 2024 Research Video Series - PTC Update September 06, 2024 Update on GENERATION HD2 September 05, 2024 Update from Prilenia September 03, 2024 Research Video Series: SURVEYOR opens the door August 30, 2024 NEW Research Video Series: The Director's Cut July 25, 2024